Enter your terms above and click the 'Search' button.

Showing articles 0 to 1 of 1 Filter Applied: efficacy (Click to remove) Lentiviral Haematopoietic stem-cell gene therapy for early-onset metachromatic leukodystrophy: long-term results from a non-randomised, open-label, phase 1/2 trial and expanded access Lancet 399:372-383, Fumagalli, F.,et al, 2022 Showing articles 0 to 1 of 1